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Lysosomal Disease Treatment Market by Disease Type (Gauchers Diseases, Fabry Diseases, Pompes Syndrome, Mucopolysaccharidosis, Aspartylglucosaminuria, Batten Disease, Cystinosis, Glycogen Storage Disease II, Tay-Sachs Disease, and Others), Therapy (Haematopoietic Stem Cell Transplantation, Enzyme Replacement Therapy, Substrate Reduction, and Chaperone Therapies), Route of Administration (Intravenous and Oral), and End User (Hospitals, Clinics, Stem Transplant Center, Research Organizations, and Others): Global Opportunity Analysis and Industry Forecast, 2019–2026

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Dec 2019 | 85 Views
 
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Lysosomal disease, also called as lysosomal storage disorder (LSD), is a group of genetic metabolic disorders, which are caused due to enzyme deficiencies within the lysosome. Lysosome is present inside a cell and aids in the breakdown of cell substances, thus speeding up the reaction in the body. Absence of lysosomal enzymes in the body lead to lysosomal disorder, which in turn results in formation of toxic substances, thereby damaging the organs of the body. Around 50 types of lysosomal storage disorders are prevalent across the globe. These may affect different parts of the body such as the skin, heart, brain, skeleton, and central nervous system. The symptoms of lysosomal disorder differ depending on variables such as age of onset, delay of the treatment, and others. Patients suffering from LSD have enlarged livers or spleens, pulmonary & cardiac problems, and bones that grow abnormally. Moreover, these symptoms are progressive over a period of time.

The lysosomal disease treatment market is expected to witness significant growth during the forecast period due to factors such as allocation of orphan drug status to drugs used for treatment of lysosomal disorder. Moreover, rise in awareness related to early diagnosis of lysosomal diseases is another major factor that contributes to the growth of lysosomal disease treatment market. Furthermore, increase in newborn screening for lysosomal diseases boosts the market growth. However, changes in payer policies and lack of skills & know-how about nature of disease are the major issues that hinder the growth of the market. On the contrary, new treatment options available for the cure of lysosomal disorders such as gene therapies is anticipated to provide lucrative opportunities for the market expansion during the forecast period.

The global lysosomal disease treatment market is segmented based on disease type, therapeutics, route of administration, end user, and region. Depending on disease types, the market is divided into gauchers diseases, fabry diseases, pompes syndrome, mucopolysaccharidosis, aspartylglucosaminuria, batten disease, cystinosis, glycogen storage disease II, tay-sachs disease, and others. On basis of therapy, it is categorized into hematopoietic stem cell transplantation, enzyme replacement therapy, substrate reduction, and chaperone therapies. By route of administration, it is bifurcated into intravenous and oral. As per end user, it is fragmented into hospitals, clinics, stem transplant center, research organizations, and others. Region wise, it is analyzed across North America (U.S., Canada, and Mexico), Europe (Germany, France, the UK, Spain Italy, and rest of Europe), Asia-Pacific (China, Japan, Australia, South Korea and rest of Asia-Pacific), and LAMEA (Brazil, South Africa, and rest of LAMEA).

KEY BENEFITS FOR STAKEHOLDERS

  • This report provides a detailed quantitative analysis of the current lysosomal disease treatment market trends and future estimations from 2019 to 2026, which assist to identify the prevailing cystic fibrosis therapeutics market opportunities. 
  • An in-depth market analysis of various regions is anticipated to provide a detailed understanding of the current trends to enable stakeholders formulate region-specific plans.
  • A comprehensive analysis of the factors that drive and restrain the growth of the global lysosomal disease treatment market is provided.
  • Region-wise and country-wise market conditions are comprehensively analyzed in this report.
  • An extensive analysis of various regions provides insights that are expected to allow companies to strategically plan their business moves.
  • Key market players within the lysosomal disease treatment market are profiled in this report and their strategies are analyzed thoroughly, which help to understand the competitive outlook. 

KEY MARKET SEGMENTS

By Disease Type

  • Gauchers Diseases
  • Fabry Diseases
  • Pompes Syndrome
  • Mucopolysaccharidosis
  • Aspartylglucosaminuria
  • Batten Disease
  • Cystinosis
  • Glycogen Storage Disease II
  • Tay-Sachs Disease 
  • Others

By Route of Administration

  • Intravenous
  • Oral

By Therapy

  • Hematopoietic Stem Cell Transplantation
  • Enzyme Replacement Therapy
  • Substrate Reduction
  • Chaperone Therapies

By End User

  • Hospitals
  • Clinics
  • Stem Transplant Center
  • Research Organizations
  • Others

By Region

  • North America
    • U.S.
    • Canada
    • Mexico
  • Europe
    • Germany
    • France
    • UK
    • Italy
    • Spain
    • Rest of Europe
  • Asia-Pacific
    • Australia
    • Japan
    • India
    • China
    • South Korea
    • Rest of Asia-Pacific
  • LAMEA
    • Brazil
    • Saudi Arabia
    • South Africa
    • Rest of LAMEA
 
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